OUR MISSION
OUR GOAL IS TO FIND A CURE FOR DEVASTATING (SO FAR) FATAL INFANT DISEASE SANFILIPPO (MPSIII).
NEWS
Heute is der Tag der Seltenen Erkrankungen. Es sind mehr Menschen betroffen als Du Dir es vorstellen kannst. Allein in Deutschland leiden 4Mio. Betroffene darunter,
Rare Disease Day 2025 official video
This year’s Rare Disease Day video highlights the inspiring journeys of four families from across the globe, united by their experiences of living with rare ...